Presenter: Rebecca Kaviani, PA-C This presentation provides a comprehensive overview of emerging gene therapy treatments for patients with sickle cell disease. Participants will explore the pathophysiology of sickle cell disease, limitations of traditional management strategies, and the clinical application of recently approved gene therapy products. Emphasis...
Presenter: Sonata Jodele, MD This session examines transplant-associated thrombotic microangiopathy (TA-TMA) as a significant complication of hematopoietic stem cell transplantation. Participants will gain an in-depth understanding of endothelial injury, disease pathophysiology, diagnostic criteria, and risk stratification. The presentation emphasizes early recognition through clinical assessment, laboratory monitoring, and...
Presenter: Stefanie Mecham, RN This presentation provides a foundational overview of pediatric stem cell transplantation, including indications, donor sources, preparatory regimens, and post-transplant care. Participants will review autologous and allogeneic transplant processes, conditioning strategies, and sources of stem cells. Common complications, supportive care needs, and long-term...
Presenter: Trish McMahon Peterson, NP This presentation focuses on the assessment and management of pediatric bone marrow failure syndromes, including acquired and inherited disorders. Participants will review diagnostic criteria, treatment pathways, and potential complications associated with bone marrow failure. Emphasis is placed on patient and family...
